Karen's Kickstarter project research
Amyloidosis : Definition by Mayo Clinic Staff
Amyloidosis (am-uh-loi-DO-sis) is a rare disease that occurs when a substance called amyloid builds up in your organs. Amyloid is an abnormal protein that is usually produced in your bone marrow and can be deposited in any tissue or organ.
Martha Grogan, M.D., Mayo Clinic cardiologist, reviews the treatment options available for patients with cardiac amyloidosis. This is part three of a series of three videos that review what every patient needs to know about cardiac amyloidosis.
Part 1: What is Amyloidosis and how does it affect the heart?
Part 2: Tests and Assessments
Part 3: Treatment Options
What Are Clinical Trials?
A critical part in the process of bringing new therapies to patients is clinical development, the study of potential new therapies in humans.
Pfizer’s Vyndaqel® (tafamidis) First Therapy Approved in the European Union for the Rare and Fatal Neurodegenerative Disease Transthyretin Familial Amyloid Polyneuropathy (TTR-FAP)
Approval Represents a Major Advance, as Vyndaqel is the First and Only Medication Currently Approved to Delay Peripheral Neurologic Impairment in Stage 1 TTR-FAP Patients (November 17, 2011)